Positive updates across all programs, including longer term efficacy and safety data from the HELIOS open-label extension trial of bitopertin in erythropoietic protoporphyria (EPP), additional ...

"Sickle cell disease is a devasting disorder that affects approximately 100,000 people in the U.S., leading to anemia, severe pain, stroke and even early death. Receiving orphan drug designation from ...

Updated Data from 17 Patients Consistent with Previously Presented Data; All Patients Treated with BEAM-101 Achieved Hemoglobin F (HbF) Induction of ...

ADMITTED to hospital with chest pains in April after suffering two major heart attacks weeks prior, Sally Wood has understandably been cautious about her health since then. But during her overnight ...

An international clinical trial co-led by Roswell Park Comprehensive Cancer Center has demonstrated that the investigational drug ziftomenib can produce deep, durable responses in people with a ...

The American Society of Hematology (ASH) and the International Society on Thrombosis and Hemostasis (ISTH) released new and updated clinical practice guidelines for the treatment of pediatric ...

Thanks to rapid drug development and expanding clinical research, patients now have access to more personalized treatment options than ever before. But for healthcare providers—doctors ...

The American Society of Hematology (ASH) and the International Society on Thrombosis and Haemostasis (ISTH) released new and updated clinical practice guidelines for the treatment of pediatric ...

LITTLE ROCK (KATV) — Emily Rogers, a 22-year-old native of Hot Springs, is battling a severe form ... treatment that's available for cell marker 22 however," said Brandy, Emily's mother. A new ...

Roswell Park's Dr. Eunice Wang delivers latest results from KOMET-001 clinical trial BUFFALO ... to standard treatments occurs within a year of treatment. At that point, outcomes are poor ...

Timely diagnosis and appropriate treatment—guided by risk stratification and clinical presentation—are essential to minimize morbidity. Primary care providers play a key role in patient ...