Elevidys (delandistrogene moxeparvovec) can now be used to treat both ambulatory and non-ambulatory boys aged four and above with DMD, a major expansion on its earlier accelerated approval with a ...

and ELEVIDYS, an adeno-associated virus based gene therapy for the treatment of ambulatory pediatric patients aged 4 through 5 years with duchenne with a confirmed mutation in the duchenne gene.

The green light for delandistrogene moxeparvovec – now given the brand name Elevidys – comes after a long and sometimes tortuous path through clinical development and an FDA advisory committee ...

Table 01: Global Glass Vials Market Historic Value (US$ Bn), By Glass Type 2015(H)-2021(A) Table 02: Global Glass Vials Market Forecast Value (US$ Bn), By Glass Type 2022(E)-2032(F) Table 03: Global ...

After hours: 4 March at 6:19:46 pm GMT-5 ...

Pfizer’s decision to halt further marketing of Beqvez is further sign of the sparse patient interest in gene therapies for the bleeding condition. Rapid scientific advances have put the gene therapy ...

A small semaglutide trial suggests the medicine's suppression of appetite may extend to alcohol, but larger tests are needed to establish a conclusive benefit.