University of California1d
Breathing new life: Working toward an inhalable gene therapy for cystic fibrosis
Although cystic fibrosis is a single gene mutation, there are more than 1,000 different ways the CFTR gene can mutate in ...
Baylor College of Medicine23d
Evenings with Genetics focuses on cystic fibrosis
Cystic fibrosis is a genetic condition that causes persistent lung infections ... Light refreshments will be provided beginning at 6:30 p.m., and the seminar will begin at 7 p.m. For more information, ...
Science Daily6d
Newly uncovered mechanism could drive next-gen cystic fibrosis treatments
The Hospital for Sick Children. "Newly uncovered mechanism could drive next-gen cystic fibrosis treatments." ScienceDaily. ScienceDaily, 13 March 2025. <www.sciencedaily.com / releases / 2025 / 03 / ...
Cystic Fibrosis Clinical Trials and Studies: EMA, PDMA, FDA Approvals, Mechanism of Action, ROA, NDA, IND, and Companies
In March 2025, Vertex Pharmaceuticals Incorporated announced a study is to evaluate the safety, and tolerability and efficacy ...
Cystic Fibrosis Foundation1d
Cystic Fibrosis Foundation Celebrates New National Volunteer Advocacy Co-Chairs
The Foundation’s National Volunteer Advocacy Committee provides guidance and support to further strengthen and enhance the ...
The Sun4d
Miracle daily pill to help condition suffered by 10,000 people could soon be available on the NHS
A MIRACLE pill that's been shown to help with many of the symptoms of cystic fibrosis (CF) has been approved for thousands of UK sufferers. The genetic condition affects over 11,000 people in the ...