Despite the recent approval of targeted biologics that can significantly improve quality of life, Canadians living with Myasthenia Gravis continue to face unjust policy barriers.

Scientists at Brigham and Women's Hospital and Harvard Medical School have developed a targeted genetic test to improve ...

A gene therapy for Duchenne muscular dystrophy caused complications to the liver, prompting a review of its use for younger patients.

When your body’s immune cells attack you instead of protecting you, today’s treatments tamp down the friendly fire but they ...

Innovation Passport award facilitates accelerated time to market and helps expedite patient access to transformative new medicines - - New ...

Because researchers have made such striking progress in developing drugs to treat neuromuscular diseases, Scott Delp, Ph.D., ...

Stanford Medicine researchers found that a smartphone could monitor patients with two types of muscular dystrophy as well as ...

You can call it a "car wash for a cause" - and it's a cause that is very close to the Pantier Family's heart. Their 8-year-old son, Christopher, is living with SMA, or spinal muscular atrophy. It's a ...

The Chaparral Football Car Wash Fundraiser for SMA is happening Saturday, October 25, from 11 a.m. to 1 p.m. at Chaparral High School in Scottsdale. All of the proceeds will be donated to the ...

Background Over the last few years, there has been increasing attention to the involvement of the central nervous system in Duchenne muscular dystrophy (DMD). The aim of this study was to assess the ...